A Promising Small Molecule for Vanishing White Matter Disease
DOI:
https://doi.org/10.15844/pedneurbriefs-32-5Keywords:
Vanishing White Matter Disease, Leukoencephalopathy, Leukodystrophy, Integrated Stress Response, Eif2b, ISRIBAbstract
Investigators from Calico Life Sciences LLC and AbbVie report the effects of a novel drug targeting the genetic basis of Vanishing White Matter Disease (VWMD).Published
2018-08-28
Issue
Section
Degenerative Diseases
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