Risk Prediction for Niemann-Pick Disease

Authors

  • J Gordon Millichap Northwestern University Feinberg School of Medicine

DOI:

https://doi.org/10.15844/pedneurbriefs-26-6-8

Keywords:

Visceral, Neurologic, Psychiatric Domains

Abstract

A retrospective chart review of 216 patients with Niemann-Pick disease type C (NP-C) was conducted in 5 centers in Europe including University of Amsterdam and 2 in Australia.

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Published

2012-06-01

Issue

Section

Metabolic Disorders